Astellas Pharma

Astellas is a global life sciences company committed to turning innovative science into VALUE for patients. We provide transformative therapies in disease areas that include oncology, ophthalmology, urology, immunology and women’s health. Through our research and development programs, we are pioneering new healthcare solutions for diseases with high unmet medical need.

At Astellas, our goal is to push the boundaries of what is possible to deliver breakthrough, first-of-their-kind gene therapies. Our gene therapy drug discovery engine is built around novel science, a validated adeno-associated virus (AAV) platform, and an industry leading internal manufacturing capability with a particular focus on rare diseases of the eye, CNS and neuromuscular system.

We are boldly forging the future of gene therapy by conducting investigational research in X-Linked Myotubular Myopathy (XLMTM) and Pompe disease. As part of our commitment to the patients and families we serve, we are constantly seeking to deepen our understanding of the lived experience of those affected by genetic disorders in order to provide access to information and resources that could be helpful to the communities we support.

Below are links to helpful resources for your practice and patients.

Resources for Patients and Families (Intended for US Audiences Only)

For more information on XLMTM: About XLMTM – Astellas Gene Therapies

For more information on Pompe Disease: Facing Pompe Together

For more information on gene therapy: What Is Gene Therapy?

Resources for US-based Healthcare Professionals:

Gene Replacement Therapy Brochure.pdf

XLMTM Disease Education Brochure.pdf

xlmtm.com

Pompe Disease Education Brochure.pdf

Therapeutic Approaches in Pompe Disease Brochure.pdf

Learn more at: Astellas Gene Therapies

Follow us on LinkedIn: https://www.linkedin.com/company/astellaspharmainc/